11 January 2017 / Posted in: Research
A potential new therapy for SMA, which could possibly be combined with other drugs such as Spinraza to enhance clinical effectiveness, has been identified and successfully tested in mouse models of the disease.
06 January 2017 / Posted in: Research
In this timely article, Dr. Alex Murphy describes the organisations involved and outlines the processes that have to be gone through before a drug can be prescribed for an individual in the UK.
04 January 2017 / Posted in: Research
Read a joint statement from SMA Support UK, Muscular Dystrophy UK and The SMA Trust.
04 January 2017 / Posted in: Information & Support
In this new SMA Voices piece, Joseph's dad, Aidan, shares his thoughts, feelings and experiences twenty years on about his son who had SMA Type 1 and sadly passed away.
22 December 2016 / Posted in: Research
Read a statement from Roche about their 2017 clinical trials of drug RG7916.
21 December 2016 / Posted in: Research
Read the report on progress towards an Expanded Access Programme of the ENDEAR trial of nusinersen which treats eligible infants with Spinal Muscular Atrophy Type 1.
15 December 2016 / Posted in: Research
Results from a phase 2 clinical trial of the Ionis Pharmaceuticals gene therapy drug, Nusinersen (now marketed as Spinraza), have been published in the medical journal The Lancet.
15 December 2016 / Posted in: Our Community
This month, we want to say a big thank you to everyone who, this year, has given their time and supported our work in so many different ways.
14 December 2016 / Posted in: Information & Support
Turn2us' poverty campaign, No Cold Homes, is running throughout the Winter and they are promoting the support available for people who can’t afford to heat their homes this Winter.
07 December 2016 / Posted in: Help Us
Martina and Glyn’s son Max had SMA Type 1 and sadly died in May this year. Glyn and friends decided to form this stylish team to raise money in Max’s memory for Welsh children’s hospice Ty Hafan and SMA Support UK.