Tel: 01789 267520

Latest News: Research

New Clinical Care Research Article: Complementary & Alternative Therapies

06 December 2016 / Posted in: Research

In Dr. Alex Murphy's latest article, he summaries some of the more common CATs (Complementary and Alternative Therapies) and looks into evidence for their use in SMA or similar conditions.

Read full story

PhD Studentships at Royal Holloway, University of London

05 December 2016 / Posted in: Research

Applications are open for PhD Studentships and one of the available projects is 'Psychosocial and ethical issues in perinatal gene and cell therapies for Spinal Muscular Atrophy'. Deadline for applications if Friday 9th December.

Read full story

Biogen and Ionis Provide Community Update on CHERISH Nusinersen Trial

08 November 2016 / Posted in: Research

Biogen and Ionis Pharmaceuticals have provided the following community statement regarding the interim analysis of the CHERISH trial.

Read full story

New Pivotal Study Announced by AveXis

07 November 2016 / Posted in: Research

AveXis has announced details about a future pivotal trial of their gene therapy drug for SMA Type 1, AVXS-101.

Read full story

FDA Accept Nusinersen For Priority Review

31 October 2016 / Posted in: Research

Biogen have announced that their New Drug Application (NDA) for Nusinersen has been accepted by the US Food and Drug Administration (FDA) for Priority Review.

Read full story

Biogen And Ionis Provide Update On European Nusinersen Approval Process

11 October 2016 / Posted in: Research

In response to requests for information, Biogen and Ionis provide an update on the progress made in moving the nusinersen development program forward.

Read full story

Views Sought On The Use Of Non-Invasive Prenatal Testing (NIPT)

06 October 2016 / Posted in: Research

The Nuffield Council on Bioethics is thinking about the ethical issues raised by NIPT and would like to talk to people over 18 who have SMA about their views on current and future uses of NIPT.

Read full story

Biogen and Ionis update on New Drug Application for Nusinersen

27 September 2016 / Posted in: Research

In response to requests for information, this update from Biogen and Ionis is for all in the SMA community.

Read full story

Roche Initiate Phase II Trial of RG7916

27 September 2016 / Posted in: Research

Roche have announced that they are to begin recruiting SMA patients in two parallel Phase II clinical trials of their second splice-modifying drug, RG7916 (also known as RO7034067).

Read full story

Molecular “Homing Devices” Drastically Improve SMA Therapy

22 September 2016 / Posted in: Research

Antisense oligonucleotide technology holds great promise for the treatment of SMA.

Read full story