Drug Treatments - What's Happening Now?
Find out more about this first USA and European approved treatment for SMA, the work we are doing to improve access in the UK, and how you can help.
Track the development of possible SMA treatments in our Drug Pipeline and learn more about some of the drugs currently being tested.
This information sheet tells you more about how trials work, what to ask, and who to speak to if you are interested in joining one.
The NICE process and what happens in the rest of the UK Last updated 11th October 2018...